Fact sheets Lupus Acromegaly Autosomal dominant polycystic kidney disease Castleman disease Cushing syndrome Primary biliary cholangitis Fabry disease See more Sandhoff disease on the forum US Approves First RNA Interference Drug What can we do to stay healthy while stuck... What is the most frustrating or difficult... How were you diagnosed with a rare disease? What is the most frustrating or difficult... How were you diagnosed with a rare disease? What can we do to stay healthy while stuck... US Approves First RNA Interference Drug See the forum Sandhoff disease Newsfeed Sandhoff disease on Sep 4, 2018 US Approves First RNA Interference Drug Read the article See more news