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Sandhoff disease
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- What can we do to stay healthy while stuck at home?
I feel discouraged about my weight loss. The best thing for me is the pool, but they are all closed.
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- US Approves First RNA Interference Drug
Alnylam’s Onpattro (patisiran) can treat a rare hereditary disease by silencing a specific gene. The first therapy based on RNA interference (RNAi) gene silencing has been approved by the US Food a
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