Ongoing discussions - Hurler syndrome
- What can we do to stay healthy while stuck at home?
I feel discouraged about my weight loss. The best thing for me is the pool, but they are all closed.
- US Approves First RNA Interference Drug
Alnylam’s Onpattro (patisiran) can treat a rare hereditary disease by silencing a specific gene. The first therapy based on RNA interference (RNAi) gene silencing has been approved by the US Food a